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Fitusiran in haemophilia:
von Willebrand factor
HISTORY
Therapy for Hemophilia A
rbd's
international registries of rare bleeding disorders.
Detection of Factor XIII deficiency
prevent major spontaneous bleeds
misdiagnosis of dysfibrinogenaemia
The European Haemophilia Network (EUHANET)
#RareDiseaseDay 2025
EAHAD 2025 Milan
EAHAD Presidential Interview: Flora Peyvandi
datasets: The SATURN methodology
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