Fitusiran in haemophilia:

Fitusiran in haemophilia: a breakthrough drug with many unknowns.

Peyvandi F, Garagiola I, Abbattista M. Lancet. 2023 Mar 29:S0140-6736(23)00514-7. doi: 10.1016/S0140-6736(23)00514-7. Online ahead of print.