The Rare Bleeding Disorders Network

EJP-RD information/networking event for the Internal call for innovation projects in clinical trials methodologies in limited populations

An “Information/Networking Event” will be held online on 25th January 2021 in the context of the EJP RD internal call for innovation projects in clinical trials methodologies in limited populations.

This event aims to present the call modalities and objectives followed by Q&A session with participants and the various perspectives of the remaining challenges that the present call will target (for example in relation to use of registries, innovation in methodology space, PCOMS, pharmacogenetic biomarkers and pharmacokinetics development, the vision of regulators on future of RD clinical trials, model for innovating therapy in ultra RDs, ethical guidance).
Open sessions are organised for participants to discuss the gaps that they would like to tackle and initiate partnerships among interested parties.